Beta-thalassemia major
Beta-thalassemia major
Definition
Beta-thalassemia (BT) major is a severe early-onset form of BT characterized by severe anemia requiring regular red blood cell transfusions.
Also known as Beta thalassemia Major, Cooley anaemia, Cooley anemia, Cooley's Anaemia, Cooley's Anemia, Mediterranean anaemia, Mediterranean anemia — per MONDO