Spinocerebellar ataxia with epilepsy

Spinocerebellar ataxia with epilepsy

Definition

A rare, mitochondrial DNA maintenance syndrome characterized by cerebellar ataxia, sensory peripheral neuropathy, myoclonus, epilepsy, progressive cognitive impairment, late-onset ptosis and external ophthalmoplegia. Liver failure may also occur, most often in association with the use of antiepileptic drug sodium valproate.

Also known as mitochondrial spinocerebellar ataxia with epilepsy, MSCAE, SCAE — per MONDO

Also identified as