Pyruvate carboxylase deficiency, benign type

Pyruvate carboxylase deficiency, benign type

Definition

Benign pyruvate carboxylase (PC) deficiency (Type C) is a rare, very mild form of PC deficiency characterized by episodic metabolic acidosis and normal or mildly delayed neurological development.

Also known as pyruvate carboxylase deficiency type C — per MONDO

Also identified as