Muscular dystrophy-dystroglycanopathy (congenital with brain and eye anomalies), type A, 4

Muscular dystrophy-dystroglycanopathy (congenital with brain and eye anomalies), type A, 4

Definition

Fukuyama type muscular dystrophy (FCMD) is a congenital progressive muscular dystrophy characterized by brain malformation (cobblestone lissencephaly), dystrophic changes in skeletal muscle, severe intellectual deficit, epilepsy and motor impairment.

Also known as FCMD, Fukuyama congenital muscular dystrophy, Fukuyama Type Congenital Muscular Dystrophy, MDDGA4, muscle-eye-brain-FKTN related, muscular dystrophy-dystroglycanopathy (congenital with Brain and eye anomalies) type A, 4, muscular dystrophy-dystroglycanopathy (congenital with brain and eye anomalies), type A, 4, Walker-Warburg syndrome or muscle-eye-brain disease, FKTN-related — per MONDO

Also identified as

Affected Organs

Organ Involvement Source
Musculature Disease Has Associated Anatomic Site NCIT · CC BY 4.0
Musculature Disease Has Primary Anatomic Site NCIT · CC BY 4.0
Musculoskeletal system Disease Has Associated Anatomic Site NCIT · CC BY 4.0
Musculoskeletal system Disease Has Primary Anatomic Site NCIT · CC BY 4.0
Nervous system Disease Has Associated Anatomic Site NCIT · CC BY 4.0
Nervous system Disease Has Primary Anatomic Site NCIT · CC BY 4.0
Peripheral nervous system Disease Has Associated Anatomic Site NCIT · CC BY 4.0
Peripheral nervous system Disease Has Primary Anatomic Site NCIT · CC BY 4.0