Myofibrillar myopathy 3
Myofibrillar myopathy 3
Definition
A rare, late adult-onset myofibrillar myopathy characterized by progressive distal muscle weakness associated with peripheral neuropathy and hyporeflexia. Ambulation may be lost within a few years.
Also known as autosomal dominant distal myopathy caused by mutation in MYOT, autosomal dominant limb-girdle muscular dystrophy caused by mutation in MYOT, autosomal dominant limb-girdle muscular dystrophy type 1A, distal myotilinopathy, LGMD1A, myofibrillar myopathy type 3, myopathy, myofibrillar, type 3, MYOT autosomal dominant distal myopathy, MYOT autosomal dominant limb-girdle muscular dystrophy, MYOT-related myofibrillar myopathy, myotilinopathy, spheroid body myopathy — per MONDO
Also identified as
- DOID 0080094 per MONDO
- DOID 0110300 per MONDO
- MESH C000598645 per MONDO
- MESH C535906 per MONDO
- MESH C563775 per MONDO
- OMIM 159000 per MONDO
- OMIM 182920 per MONDO
- OMIM 609200 per MONDO
- Orphanet 266 per MONDO
- Orphanet 268129 per MONDO
- Orphanet 98911 per MONDO
- SCTID 719985001 per MONDO
- SCTID 765092004 per MONDO
- SCTID 765196004 per MONDO
- UMLS C3714934 per MONDO