Gaucher disease

ICD-10 Code E75.22

Gaucher disease

Definition

Gaucher disease (GD) is a lysosomal storage disorder encompassing three main forms (types 1, 2 and 3), a fetal form and a variant with cardiac involvement (Gaucher disease - ophthalmoplegia - cardiovascular calcification or Gaucher-like disease).

Also known as acid beta-glucosidase deficiency, Gaucher disease, Gaucher syndrome, glucocerebrosidase deficiency, glucocerebrosidosis, glucosylceramidase deficiency, glucosylceramide beta-glucosidase deficiency, lipoid histiocytosis (kerasin type) — per MONDO

Also identified as

Drugs indicated

Drug Relation Source
Cycloserine may treat MEDRT · Public domain (U.S. Government work)
Eliglustat may treat MEDRT · Public domain (U.S. Government work)
Miglustat may treat MEDRT · Public domain (U.S. Government work)